Tag: Rare Diseases

$27.7 Million Project to Advance Gene-Editing Therapies for Rare Immune Diseases

Mayo Clinic joins a $27.7 million ARPA-H project using CRISPR gene editing…

ME Desk

Dubai Ruler to Fund Treatment for Jordanian Girl with Spinal Muscular Atrophy

Dubai Ruler to fund treatment for 1-year-old Jordanian girl Katya Abu Al-Saud,…

ME Desk

Abu Dhabi Doctors Perform Life-Saving Bone Marrow Transplant for Toddler

Abu Dhabi doctors successfully treat a 13-month-old with rare Omenn Syndrome through…

ME Desk

SSMC Treats Rare Vascular Condition with Robotic-Assisted Surgery in Abu Dhabi

SSMC in Abu Dhabi successfully treats a rare vascular condition using robotic-assisted…

ME Desk

Lacutamab Advances Toward Phase 3 Trial in T-Cell Lymphoma

Sobi and Innate Pharma partner to advance lacutamab into a Phase 3…

ME Desk

Abu Dhabi Stem Cells Center Achieves Major Scientific Breakthrough in Huntington’s Disease Research

Abu Dhabi Stem Cells Center reports a breakthrough in Huntington's disease research,…

ME Desk

Abu Dhabi Activates Rare Diseases Centre of Excellence

The Department of Health โ€“ Abu Dhabi, AstraZeneca, and PureHealth have partnered…

ME Desk