Tag: Rare Diseases

Novel Drug Therapy Offers Hope for Children With Brain-Injury-Related Obesity, Study Finds

Sidra Medicine has published a groundbreaking case report highlighting the successful use…

ME Desk

Vertex Presents New CASGEVY Data in Children, Expands Global Regulatory Filings

Vertex Pharmaceuticals presented new data showing positive outcomes with CASGEVY in children…

ME Desk

Sanofi provides update on MOBILIZE phase 3 study of riliprubart in chronic inflammatory demyelinating polyneuropathy

Sanofi has announced the discontinuation of its Phase 3 MOBILIZE study evaluating…

ME Desk

Nivey Nocher Joins The PHA Group to Lead Health Department

The PHA Group has appointed Nivey Nocher as Executive Vice President, Health,…

ME Desk

Pfizer Reaches Three Settlement Agreements for VYNDAMAX

Pfizer has reached settlement agreements with multiple generic manufacturers over VYNDAMAX (tafamidis),…

ME Desk

Advancing Sickle Cell Cure in Africa: Transplant & Gene Therapy | Dr. Lawrence Faulkner | BMT

Advances in transplant medicine and gene editing are reshaping the future of…

ME Desk

KFSH Successfully Implements Gene Therapy for Sickle Cell Disease

King Faisal Specialist Hospital & Research Centre (KFSH) successfully implements gene therapy…

ME Desk

Understanding Rare Diseases in the MENA Region

Rare diseases affect millions across the MENA region, yet diagnosis, treatment access,…

Dr. Khedidja Hedna

Why Cervical Cancer Is More Preventable Than Many Realise

Cervical cancer remains one of the most preventable yet overlooked health risks…

Harshad Hussain B