In this insightful interview, Dr. Zainul Aabideen speaks with Prof. Stephan Grupp, a leading expert in pediatric oncology and gene therapy at the Children’s Hospital of Philadelphia. Prof. Grupp explains the principles of gene therapy, how it works for diseases like Sickle Cell and Thalassemia, and discusses the latest advancements in this groundbreaking field. He also addresses the challenges of accessibility and cost, and shares his vision for the future of gene therapy for children worldwide.
Key topics covered:
- What is gene therapy and how does it work?
- FDA-approved gene therapy treatments for various conditions
- Differences between direct gene therapy and cell modification approaches
- Short-term and long-term effects of treatment
- Current challenges of cost and accessibility
- Future outlook for making gene therapy available worldwide
#mededgemea #GeneTherapy #PediatricOncology #SickleCell #Thalassemia #HealthcareInnovation #MedicalAdvancements #ChildrensHealth MENA Conference Society of Critical Care Medicine
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